Gabby Zeppieri, has been diagnosed with Neutral Lipid Storage Disease with Myopathy (NLSD-M), an ultra rare and genetic disease. This disease is a progressive and debilitating disease that stores lipids in the skeletal muscles. Gabby has developed severe weakness in her upper and lower extremities. This condition has drastically affected Gabby's day to day functioning.

While the prognosis is challenging, there is new hope: Gabby has the opportunity to participate in Phase 1 of a groundbreaking gene therapy treatment. This treatment could be life-changing for her and others suffering with this disease, but as you can imagine, it comes with a significant cost.

To give Gabby and all patients diagnosed with NLSD-M the chance they all deserve, we need to raise $125,000. These funds will be applied towards the initial phase of this gene therapy project. This is where we need your help. Gabby's Wonderful World foundation is looking to provide funds raised as a grant to the Center for Gene Therapy at Nationwide Children’s Hospital for the gene PNPLA2 disease research and therapy development.

How You Can Help:

Donate: Every contribution, no matter the size, brings us closer to our goal. Gabby's Wonderful World is a 501 (c)(3) non profit organization. All donations from within the US are tax deductible.
Share: Spread the word. The more people who hear about Gabby’s story, the better our chances of reaching our target.

Gabby is a fighter, and this treatment represents not just hope, but a new beginning for all of those individuals diagnosed with NLSD-M. Your support, whether through donations or simply by sharing this campaign, means the world to us and will make all the difference in our journey.

We will be sharing updates along the way, and we can’t wait to keep you all involved in this life-changing process.

Thank you from the bottom of our hearts for your generosity and support.

With love and gratitude,
Gabby’s Wonderful World

Development of a Gene Therapy Treatment for Neutral Lipid Storage Disease with Myopathy

By Gww Nlsdm Corp

Development of a Gene Therapy Treatment for Neutral Lipid Storage Disease with Myopathy

Gabby's Fight is Our Fight! Help Fund a Cure for NLSD-M.